| Endogenous microRNA can be broadly exploited to regulate transgene expression according to tissue, lineage and differentiation state BD Brown, B Gentner, A Cantore, S Colleoni, M Amendola, A Zingale, ... Nature biotechnology 25 (12), 1457-1467, 2007 | 669 | 2007 |
| Site-specific integration and tailoring of cassette design for sustainable gene transfer A Lombardo, D Cesana, P Genovese, B Di Stefano, E Provasi, ... Nature methods 8 (10), 861-869, 2011 | 388 | 2011 |
| A microRNA-regulated lentiviral vector mediates stable correction of hemophilia B mice BD Brown, A Cantore, A Annoni, LS Sergi, A Lombardo, P Della Valle, ... Blood, The Journal of the American Society of Hematology 110 (13), 4144-4152, 2007 | 340 | 2007 |
| In vivo delivery of a microRNA-regulated transgene induces antigen-specific regulatory T cells and promotes immunologic tolerance A Annoni, BD Brown, A Cantore, LS Sergi, L Naldini, MG Roncarolo Blood, The Journal of the American Society of Hematology 114 (25), 5152-5161, 2009 | 180 | 2009 |
| Hepatocyte‐targeted expression by integrase‐defective lentiviral vectors induces antigen‐specific tolerance in mice with low genotoxic risk J Mátrai, A Cantore, CC Bartholomae, A Annoni, W Wang, ... Hepatology 53 (5), 1696-1707, 2011 | 156 | 2011 |
| Liver-directed lentiviral gene therapy in a dog model of hemophilia B A Cantore, M Ranzani, CC Bartholomae, M Volpin, PD Valle, F Sanvito, ... Science translational medicine 7 (277), 277ra28-277ra28, 2015 | 145 | 2015 |
| Hyperfunctional coagulation factor IX improves the efficacy of gene therapy in hemophilic mice A Cantore, N Nair, P Della Valle, M Di Matteo, J Matrai, F Sanvito, ... Blood, The Journal of the American Society of Hematology 120 (23), 4517-4520, 2012 | 105 | 2012 |
| Insulin B chain 9–23 gene transfer to hepatocytes protects from type 1 diabetes by inducing Ag-specific FoxP3+ Tregs M Akbarpour, KS Goudy, A Cantore, F Russo, F Sanvito, L Naldini, ... Science Translational Medicine 7 (289), 289ra81-289ra81, 2015 | 75 | 2015 |
| Liver gene therapy by lentiviral vectors reverses anti‐factor IX pre‐existing immunity in haemophilic mice A Annoni, A Cantore, P Della Valle, K Goudy, M Akbarpour, F Russo, ... EMBO molecular medicine 5 (11), 1684-1697, 2013 | 67 | 2013 |
| Genome editing for scalable production of alloantigen‐free lentiviral vectors for in vivo gene therapy M Milani, A Annoni, S Bartolaccini, M Biffi, F Russo, T Di Tomaso, ... EMBO molecular medicine 9 (11), 1558-1573, 2017 | 53 | 2017 |
| Vector production A Cantore, AL Lombardo, L Naldini US Patent 10,912,824, 2021 | 6 | 2021 |
| Gene vector for inducing transgene-specific immune tolerance A Annoni, A Cantore, L Naldini, MG Roncarolo US Patent 9,938,540, 2018 | 5 | 2018 |
