| The neurotropic properties of AAV-PHP. B are limited to C57BL/6J mice J Hordeaux, Q Wang, N Katz, EL Buza, P Bell, JM Wilson Molecular Therapy 26 (3), 664-668, 2018 | 371 | 2018 |
| The GPI-linked protein LY6A drives AAV-PHP. B transport across the blood-brain barrier J Hordeaux, Y Yuan, PM Clark, Q Wang, RA Martino, JJ Sims, P Bell, ... Molecular Therapy 27 (5), 912-921, 2019 | 189 | 2019 |
| Adeno-associated virus-induced dorsal root ganglion pathology J Hordeaux, EL Buza, C Dyer, T Goode, TW Mitchell, L Richman, ... Human gene therapy 31 (15-16), 808-818, 2020 | 160 | 2020 |
| MicroRNA-mediated inhibition of transgene expression reduces dorsal root ganglion toxicity by AAV vectors in primates J Hordeaux, EL Buza, B Jeffrey, C Song, T Jahan, Y Yuan, Y Zhu, P Bell, ... Science translational medicine 12 (569), eaba9188, 2020 | 113 | 2020 |
| Toxicology study of intra-cisterna magna adeno-associated virus 9 expressing human alpha-L-iduronidase in rhesus macaques J Hordeaux, C Hinderer, T Goode, N Katz, EL Buza, P Bell, R Calcedo, ... Molecular Therapy Methods & Clinical Development 10, 79-88, 2018 | 90 | 2018 |
| Toxicology study of intra-cisterna magna adeno-associated virus 9 expressing iduronate-2-sulfatase in rhesus macaques J Hordeaux, C Hinderer, T Goode, EL Buza, P Bell, R Calcedo, ... Molecular Therapy Methods & Clinical Development 10, 68-78, 2018 | 74 | 2018 |
| Efficient central nervous system AAVrh10-mediated intrathecal gene transfer in adult and neonate rats J Hordeaux, L Dubreil, J Deniaud, F Iacobelli, S Moreau, M Ledevin, ... Gene therapy 22 (4), 316-324, 2015 | 73 | 2015 |
| Safe and sustained expression of human iduronidase after intrathecal administration of adeno-associated virus serotype 9 in infant rhesus monkeys J Hordeaux, C Hinderer, EL Buza, JP Louboutin, T Jahan, P Bell, ... Human Gene Therapy 30 (8), 957-966, 2019 | 66 | 2019 |
| Safe and sustained expression of human iduronidase after intrathecal administration of adeno-associated virus serotype 9 in infant rhesus monkeys J Hordeaux, C Hinderer, EL Buza, JP Louboutin, T Jahan, P Bell, ... Human Gene Therapy 30 (8), 957-966, 2019 | 66 | 2019 |
| Long-term neurologic and cardiac correction by intrathecal gene therapy in Pompe disease J Hordeaux, L Dubreil, C Robveille, J Deniaud, Q Pascal, B Dequeant, ... Acta Neuropathologica Communications 5, 1-19, 2017 | 66 | 2017 |
| Intra-CSF AAV9 and AAVrh10 administration in nonhuman primates: promising routes and vectors for which neurological diseases? K Bey, J Deniaud, L Dubreil, B Joussemet, J Cristini, C Ciron, J Hordeaux, ... Molecular Therapy Methods & Clinical Development 17, 771-784, 2020 | 64 | 2020 |
| Efficacy and safety of a Krabbe disease gene therapy J Hordeaux, BA Jeffrey, J Jian, GR Choudhury, K Michalson, TW Mitchell, ... Human gene therapy 33 (9-10), 499-517, 2022 | 26 | 2022 |
| Colorectal hamartomatous polyposis and ganglioneuromatosis in a dog I Bemelmans, S Küry, O Albaric, J Hordeaux, L Bertrand, F Nguyen, ... Veterinary pathology 48 (5), 1012-1015, 2011 | 24 | 2011 |
| Standardized method for intra-cisterna magna delivery under fluoroscopic guidance in nonhuman primates N Katz, T Goode, C Hinderer, J Hordeaux, JM Wilson Human Gene Therapy Methods 29 (5), 212-219, 2018 | 18 | 2018 |
| Inactivation of the interleukin-22 pathway in the airways of cystic fibrosis patients A Guillon, D Brea, E Luczka, V Herve, S Hasanat, C Thorey, M Pérez-Cruz, ... Cytokine 113, 470-474, 2019 | 12 | 2019 |
| Dose escalation study to evaluate safety, tolerability and efficacy of intravenous etoposide phosphate administration in 27 dogs with multicentric lymphoma P Boyé, F Serres, L Marescaux, J Hordeaux, E Bouchaert, B Gomes, ... PLoS One 12 (5), e0177486, 2017 | 10 | 2017 |
| Chronic traumatic brain injury in a dog S Laurent, JL Thibaud, J Hordeaux, E Reyes-Gomez, F Delisle, S Blot, ... Journal of comparative pathology 143 (1), 75-80, 2010 | 9 | 2010 |
| Histopathologic changes of the ear in canine models of mucopolysaccharidosis types I and VII J Hordeaux, J Deniaud, I Bemelmans, L Bertrand, S Moreau, J Amiaud, ... Veterinary pathology 48 (3), 616-626, 2011 | 8 | 2011 |
| Immune transgene-dependent myocarditis in macaques after systemic administration of adeno-associated virus expressing human acid alpha-glucosidase J Hordeaux, A Ramezani, S Tuske, N Mehta, C Song, A Lynch, K Lupino, ... Frontiers in Immunology 14, 1094279, 2023 | 7 | 2023 |
| Randomized, double-blind trial of F14512, a polyamine-vectorized anticancer drug, compared with etoposide phosphate, in dogs with naturally occurring lymphoma P Boyé, F Floch, F Serres, Z Segaoula, J Hordeaux, Q Pascal, V Coste, ... Oncotarget 11 (7), 671, 2020 | 6 | 2020 |
